Thank you for your interest in our momentous journey of developing more CFTR modulator options for people with CF.
Available clinical trials
Phase 2 study in adults with CF evaluating:
double combination of corrector PTI-801 and potentiator PTI-808 and triple combination of corrector PTI-801, potentiator PTI-808 and amplifier PTI-428.
Phase 1 study in adults with CF evaluating:
double combination of corrector PTI-801 and potentiator PTI-808.
Personalized medicine in Cystic Fibrosis
The goal of personalized medicine efforts in Cystic Fibrosis is to tailor treatment regimens for individuals based on how well they respond to drugs in a laboratory test. It remains to be seen if an in vitro response is predictive of clinical efficacy for people with Cystic Fibrosis